CLINICAL TRIALS AND OBSERVATIONS Multicenter phase 3 study of the complement inhibitor eculizumab for the treatment of patients with paroxysmal nocturnal hemoglobinuria

نویسندگان

  • Robert A. Brodsky
  • Neal S. Young
  • Elisabetta Antonioli
  • Antonio M. Risitano
  • Hubert Schrezenmeier
  • Jörg Schubert
  • Anna Gaya
  • Luke Coyle
  • Carlos de Castro
  • Chieh-Lin Fu
  • Jaroslaw P. Maciejewski
  • Monica Bessler
  • Henk-André Kroon
  • Russell P. Rother
  • Peter Hillmen
چکیده

1Johns Hopkins School of Medicine, Baltimore, MD; 2National Heart, Lung, and Blood Institute, Bethesda, MD; 3University of Florence, Florence, Italy; 4Federico II University of Naples, Naples, Italy; 5Institute of Transfusion Medicine, University Hospital Institute of Clinical Transfusion Medicine and Immunogenetics, Ulm; DRK-Blood Donor Service Baden-Württemberg-Hessen, Germany; 6Saarland University Medical School, Homburg-Saarland, Germany; 7Hospital Clinic of Barcelona, Institut d’Investigacions Biomedique Augist Pi i Sunyer (IDIBAPS), Barcelona, Spain; 8Royal North Shore Hospital, St Leonards, Australia; 9Duke University Medical Center, Durham, NC; 10Cleveland Clinic Florida, Weston, FL; 11Taussig Cancer Center, Cleveland Clinic, OH; 12Washington University in St Louis, MO; 13Alexion Pharmaceuticals, Cheshire, CT; and 14St James’s Institute of Oncology, Leeds, United Kingdom

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تاریخ انتشار 2008